Viruses Used for Gene Therapy in Sickle Cell Anemia

Sickle cell anemia affects many populations with a genetic deficiency that prevents proper formation of hemoglobin. But today, researchers are using gene therapy that actually corrects the DNA to form the oxygen carrying protein. By injecting millions of nonlethal viruses that carry the mechanism for inserting the correct genetic sequence, patients are showing that they no longer need the injectable medications that helped them with their symptoms, medications that over a lifetime may cost over $100,000. This breakthrough using CRISPR technology is being researched for other diseases and may have a tremendous role in aging overall as well.